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Aarskog-Scott syndrome: clinical and molecular characterisation of a family with the coexistence of a novel FGD1 mutation and 16p13.11-p12.3 microduplication

Aarskog-Scott syndrome (AAS), also known as facio-genital dysplasia or faciodigitogenital syndrome, is a rare genetic disorder clinically characterised by facial, limb and genitalanomalies. Although also autosomal dominance and recessive patterns have been reported, up to now, only an X linked form...

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Detalhes bibliográficos
Publicado no:BMJ Case Rep
Main Authors: Pavone, Piero, Marino, Silvia, Maniaci, Antonino, Cocuzza, Salvatore
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7328892/
https://ncbi.nlm.nih.gov/pubmed/32606125
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/bcr-2020-235183
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