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High content drug screening for Fanconi anemia therapeutics

BACKGROUND: Fanconi anemia is a rare disease clinically characterized by malformations, bone marrow failure and an increased risk of solid tumors and hematologic malignancies. The only therapies available are hematopoietic stem cell transplantation for bone marrow failure or leukemia, and surgical r...

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Foilsithe in:Orphanet J Rare Dis
Main Authors: Montanuy, Helena, Camps-Fajol, Cristina, Carreras-Puigvert, Jordi, Häggblad, Maria, Lundgren, Bo, Aza-Carmona, Miriam, Helleday, Thomas, Minguillón, Jordi, Surrallés, Jordi
Formáid: Artigo
Teanga:Inglês
Foilsithe: BioMed Central 2020
Ábhair:
Rochtain Ar Líne:https://ncbi.nlm.nih.gov/pmc/articles/PMC7325660/
https://ncbi.nlm.nih.gov/pubmed/32605631
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-01437-1
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