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Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation
Hemoglobinopathies are among the most common monogenic diseases worldwide. Approximately 1–5% of the global population are carriers for a genetic thalassemia mutation. The thalassemias are characterized by autosomal recessive inherited defects in the production of hemoglobin. They are highly prevale...
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| Publicat a: | Drugs |
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| Autors principals: | , , , |
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Springer International Publishing
2020
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| Matèries: | |
| Accés en línia: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7299245/ https://ncbi.nlm.nih.gov/pubmed/32557398 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s40265-020-01341-9 |
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