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Correction of muscular dystrophies by CRISPR gene editing

Muscular dystrophies are debilitating disorders that result in progressive weakness and degeneration of skeletal muscle. Although the genetic mutations and clinical abnormalities of a variety of neuromuscular diseases are well known, no curative therapies have been developed to date. The advent of g...

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Detalles Bibliográficos
Publicado en:J Clin Invest
Autores principales: Chemello, Francesco, Bassel-Duby, Rhonda, Olson, Eric N.
Formato: Artigo
Lenguaje:Inglês
Publicado: American Society for Clinical Investigation 2020
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7259998/
https://ncbi.nlm.nih.gov/pubmed/32478678
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI136873
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