First 1.5 years of pegvaliase clinic: Experiences and outcomes

We present Boston Children's Hospital's clinic model for pegvaliase therapy in adults with phenylketonuria (PKU) and clinical outcomes in 46 patients over the first 1.5 years of commercial therapy. Approximately 70% (18/26) of patients starting pegvaliase achieved blood phenylalanine (Phe)...

Full beskrivning

Sparad:
Bibliografiska uppgifter
I publikationen:Mol Genet Metab Rep
Huvudupphovsmän: Sacharow, Stephanie, Papaleo, Cassandra, Almeida, Kyla, Goodlett, Benjamin, Kritzer, Amy, Levy, Harvey, Martell, Leslie, Wessel, Ann, Viau, Krista
Materialtyp: Artigo
Språk:Inglês
Publicerad: Elsevier 2020
Ämnen:
Short Communication
Länkar:https://ncbi.nlm.nih.gov/pmc/articles/PMC7256053/
https://ncbi.nlm.nih.gov/pubmed/32489881
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2020.100603
Taggar: Lägg till en tagg
Inga taggar, Lägg till första taggen!

Liknande verk