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First 1.5 years of pegvaliase clinic: Experiences and outcomes

We present Boston Children's Hospital's clinic model for pegvaliase therapy in adults with phenylketonuria (PKU) and clinical outcomes in 46 patients over the first 1.5 years of commercial therapy. Approximately 70% (18/26) of patients starting pegvaliase achieved blood phenylalanine (Phe)...

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Bibliografiske detaljer
Main Authors: Stephanie Sacharow, Cassandra Papaleo, Kyla Almeida, Benjamin Goodlett, Amy Kritzer, Harvey Levy, Leslie Martell, Ann Wessel, Krista Viau
Format: Artigo
Sprog:Inglês
Udgivet: Elsevier 2020-09-01
Serier:Molecular Genetics and Metabolism Reports
Online adgang:http://www.sciencedirect.com/science/article/pii/S2214426920300495
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