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TRUST4RD: tool for reducing uncertainties in the evidence generation for specialised treatments for rare diseases

BACKGROUND: Many treatments developed for rare diseases will have an Orphan Medicinal Product (OMP) designation, indicating that they are likely to deliver benefit in an area of high unmet need. Their approval may be based on a small or uncontrolled trial, as randomised controlled trials (RCTs) of s...

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Podrobná bibliografie
Vydáno v:Orphanet J Rare Dis
Hlavní autoři: Annemans, Lieven, Makady, Amr
Médium: Artigo
Jazyk:Inglês
Vydáno: BioMed Central 2020
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7251888/
https://ncbi.nlm.nih.gov/pubmed/32456653
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-01370-3
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