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CRISPR/Cas9 Editing for Gaucher Disease Modelling

Gaucher disease (GD) is an autosomal recessive lysosomal storage disorder caused by mutations in the acid β-glucosidase gene (GBA1). Besides causing GD, GBA1 mutations constitute the main genetic risk factor for developing Parkinson’s disease. The molecular basis of neurological manifestations in GD...

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Bibliografiske detaljer
Udgivet i:Int J Mol Sci
Main Authors: Pavan, Eleonora, Ormazabal, Maximiliano, Peruzzo, Paolo, Vaena, Emilio, Rozenfeld, Paula, Dardis, Andrea
Format: Artigo
Sprog:Inglês
Udgivet: MDPI 2020
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7246564/
https://ncbi.nlm.nih.gov/pubmed/32380730
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21093268
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