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NGLY1 deficiency—A rare congenital disorder of deglycosylation

Pathogenic variants in the NGLY1 gene are associated with a Congenital Disorder of Deglycosylation (CDDG) characterized by delays in reaching developmental milestones, complex hyperkinetic movement disorder, transient elevation of transaminases, and alacrima or hypolacrima. To date, only few cases o...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:JIMD Rep
Egile Nagusiak: Lipari Pinto, Patrícia, Machado, Catarina, Janeiro, Patrícia, Dupont, Juliette, Quintas, Sofia, Sousa, Ana Berta, Gaspar, Ana
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: John Wiley & Sons, Inc. 2020
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7203651/
https://ncbi.nlm.nih.gov/pubmed/32395402
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jmd2.12108
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