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Combined Use of CFTR Correctors in LGMD2D Myotubes Improves Sarcoglycan Complex Recovery

Sarcoglycanopathies are rare limb girdle muscular dystrophies, still incurable, even though symptomatic treatments may slow down the disease progression. Most of the disease-causing defects are missense mutations leading to a folding defective protein, promptly removed by the cell’s quality control,...

Ausführliche Beschreibung

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Bibliographische Detailangaben
Veröffentlicht in:Int J Mol Sci
Hauptverfasser: Carotti, Marcello, Scano, Martina, Fancello, Irene, Richard, Isabelle, Risato, Giovanni, Bensalah, Mona, Soardi, Michela, Sandonà, Dorianna
Format: Artigo
Sprache:Inglês
Veröffentlicht: MDPI 2020
Schlagworte:
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC7084537/
https://ncbi.nlm.nih.gov/pubmed/32155735
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21051813
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