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Research priorities for liver glycogen storage disease: An international priority setting partnership with the James Lind Alliance

The international liver glycogen storage disease (GSD) priority setting partnership (IGSDPSP) was established to identify the top research priorities in this area. The multiphase methodology followed the principles of the James Lind Alliance (JLA) guidebook. An international scoping survey in seven...

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Detalles Bibliográficos
Publicado en:J Inherit Metab Dis
Main Authors: Peeks, Fabian, Boonstra, Willemijn F., de Baere, Lut, Carøe, Camilla, Casswall, Thomas, Cohen, Damián, Cowan, Katherine, Ferrecchia, Iris, Ferriani, Alberto, Gimbert, Caroline, Landgren, Marcus, Maldonado, Nerea L., McMillan, Jason, Nemeth, Antal, Seidita, Niccolò, Stachelhaus‐Theimer, Ute, Weinstein, David A., Derks, Terry G. J.
Formato: Artigo
Idioma:Inglês
Publicado: John Wiley & Sons, Inc. 2019
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7079148/
https://ncbi.nlm.nih.gov/pubmed/31587328
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jimd.12178
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