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A civil society view of rare disease public policy in six Latin American countries

Patients with rare diseases across the world struggle to access timely diagnosis and state-of-the-art treatment and management of their conditions. Several recently published reviews highlight the importance of country efforts to address rare diseases and orphan drugs policy comprehensively. However...

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Pubblicato in:Orphanet J Rare Dis
Autori principali: Mayrides, Mo, Ruiz de Castilla, Eva Maria, Szelepski, Silvina
Natura: Artigo
Lingua:Inglês
Pubblicazione: BioMed Central 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7047392/
https://ncbi.nlm.nih.gov/pubmed/32106873
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-1314-z
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