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Transduction Efficiency of Adeno-Associated Virus Serotypes After Local Injection in Mouse and Human Skeletal Muscle

The adeno-associated virus (AAV) vector is an efficient tool for gene delivery in skeletal muscle. AAV-based therapies show promising results for treatment of various genetic disorders, including muscular dystrophy. These dystrophies represent a heterogeneous group of diseases affecting muscles and...

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Dades bibliogràfiques
Publicat a:Hum Gene Ther
Autors principals: Muraine, Laura, Bensalah, Mona, Dhiab, Jamila, Cordova, Gonzalo, Arandel, Ludovic, Marhic, Alix, Chapart, Maud, Vasseur, Stéphane, Benkhelifa-Ziyyat, Sofia, Bigot, Anne, Butler-Browne, Gillian, Mouly, Vincent, Negroni, Elisa, Trollet, Capucine
Format: Artigo
Idioma:Inglês
Publicat: Mary Ann Liebert, Inc., publishers 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7047108/
https://ncbi.nlm.nih.gov/pubmed/31880951
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2019.173
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