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The Value of Imaging and Composition-Based Biomarkers in Duchenne Muscular Dystrophy Clinical Trials

As the drug development pipeline for Duchenne muscular dystrophy (DMD) rapidly advances, clinical trial outcomes need to be optimized. Effective assessment of disease burden, natural history progression, and response to therapy in clinical trials for Duchenne muscular dystrophy are critical factors...

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Pubblicato in:Neurotherapeutics
Autori principali: Chrzanowski, Stephen M., Darras, Basil T., Rutkove, Seward B.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer International Publishing 2019
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7007477/
https://ncbi.nlm.nih.gov/pubmed/31879850
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13311-019-00825-1
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