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Electrical impedance myography for reducing sample size in Duchenne muscular dystrophy trials

OBJECTIVE: To evaluate the sensitivity of electrical impedance myography (EIM) to disease progression in both ambulatory and non‐ambulatory boys with DMD. METHODS AND PARTICIPANTS: A non‐blinded, longitudinal cohort study of 29 ambulatory and 15 non‐ambulatory boys with DMD and age‐similar healthy b...

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Dades bibliogràfiques
Publicat a:Ann Clin Transl Neurol
Autors principals: Leitner, Melanie L., Kapur, Kush, Darras, Basil T., Yang, Michele, Wong, Brenda, Dalle Pazze, Laura, Florence, Julaine, Buck, Martin, Freedman, Laura, Bohorquez, Jose, Rutkove, Seward, Zaidman, Craig
Format: Artigo
Idioma:Inglês
Publicat: John Wiley and Sons Inc. 2019
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6952321/
https://ncbi.nlm.nih.gov/pubmed/31876124
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.50958
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