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Neutropenia in Glycogen Storage Disease Ib (GSD Ib): Outcomes for Patients Treated with Granulocyte Colony-Stimulating Factor (G-CSF)

GSD Ib is a complex disorder of glucose metabolism causing severe chronic neutropenia. G-CSF is effective to raise blood neutrophil counts and reduce fevers and infections in most patients. In conjunction with other therapies (salicylates, mesalamine sulfasalazine and prednisone), G-CSF ameliorates...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Julkaisussa:Curr Opin Hematol
Päätekijät: Dale, David C., Bolyard, Audrey Anna, Marrero, Tracy, Kelley, Merideth L., Makaryan, Vahagn, Tran, Emily, Leung, Jamie, Boxer, Laurence A., Kishnani, Priya S., Austin, Stephanie, Wanner, Corbinian, Ferrecchia, Iris A., Khalaf, Dina, Maze, Dawn, Kurtzberg, Joanne, Zeidler, Cornelia, Welte, Karl, Weinstein, David A.
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: 2019
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC7000169/
https://ncbi.nlm.nih.gov/pubmed/30451720
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MOH.0000000000000474
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