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Neutropenia in Glycogen Storage Disease Ib (GSD Ib): Outcomes for Patients Treated with Granulocyte Colony-Stimulating Factor (G-CSF)

GSD Ib is a complex disorder of glucose metabolism causing severe chronic neutropenia. G-CSF is effective to raise blood neutrophil counts and reduce fevers and infections in most patients. In conjunction with other therapies (salicylates, mesalamine sulfasalazine and prednisone), G-CSF ameliorates...

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Detalhes bibliográficos
Publicado no:Curr Opin Hematol
Main Authors: Dale, David C., Bolyard, Audrey Anna, Marrero, Tracy, Kelley, Merideth L., Makaryan, Vahagn, Tran, Emily, Leung, Jamie, Boxer, Laurence A., Kishnani, Priya S., Austin, Stephanie, Wanner, Corbinian, Ferrecchia, Iris A., Khalaf, Dina, Maze, Dawn, Kurtzberg, Joanne, Zeidler, Cornelia, Welte, Karl, Weinstein, David A.
Formato: Artigo
Idioma:Inglês
Publicado em: 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7000169/
https://ncbi.nlm.nih.gov/pubmed/30451720
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MOH.0000000000000474
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