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Zebrafish Models of Diamond-Blackfan Anemia: A Tool for Understanding the Disease Pathogenesis and Drug Discovery

Diamond-Blackfan anemia (DBA) is a rare bone marrow failure syndrome characterized by red blood cell aplasia. Currently, mutations in 19 ribosomal protein genes have been identified in patients. However, the pathogenic mechanism of DBA remains unknown. Recently, several DBA models were generated in...

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Detalhes bibliográficos
Publicado no:Pharmaceuticals (Basel)
Main Authors: Uechi, Tamayo, Kenmochi, Naoya
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6958429/
https://ncbi.nlm.nih.gov/pubmed/31600948
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ph12040151
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