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Spinal Muscular Atrophy Diagnosed by Newborn Screening
A panel of experts representing academic centers, family foundations and pharmaceutical industry came together to formulate a treatment algorithm for infants diagnosed via newborn screening (NBS) with Spinal muscular atrophy (SMA).
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| Publicado en: | Pediatr Neurol Briefs |
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| Main Authors: | , , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado: |
Pediatric Neurology Briefs Publishers
2019
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| Assuntos: | |
| Acceso en liña: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6942550/ https://ncbi.nlm.nih.gov/pubmed/31929716 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.15844/pedneurbriefs-33-5 |
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