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Current and emerging therapies in Becker muscular dystrophy (BMD)

Becker muscular dystrophy (BMD) has onset usually in childhood, frequently by 11 years. BMD can present in several ways such as waddling gait, exercise related cramps with or without myoglobinuria. Rarely cardiomyopathy might be the presenting feature. The evolution is variable. BMD is caused by dys...

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Dettagli Bibliografici
Pubblicato in:Acta Myol
Autori principali: ANGELINI, CORRADO, MAROZZO, ROBERTA, PEGORARO, VALENTINA
Natura: Artigo
Lingua:Inglês
Pubblicazione: Pacini Editore srl 2019
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6859412/
https://ncbi.nlm.nih.gov/pubmed/31788661
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