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Identification of mutations in Malaysian patients with argininosuccinate lyase (ASL) deficiency

Argininosuccinate lyase (ASL) deficiency impairs the function of the urea cycle that detoxifies blood ammonia in the body. Mutation that occurs in the ASL gene is the cause of occurrence of ASL deficiency (ASLD). This deficiency causes hyperammonemia, hepatopathy and neurodevelopmental delay in pati...

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Publicat a:Mol Genet Metab Rep
Autors principals: Ali, Ernie Zuraida, Yakob, Yusnita, Ngu, Lock Hock
Format: Artigo
Idioma:Inglês
Publicat: Elsevier 2019
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6831900/
https://ncbi.nlm.nih.gov/pubmed/31709144
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgmr.2019.100525
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