Curing Hemoglobinopathies: Challenges and Advances of Conventional and New Gene Therapy Approaches

Inherited hemoglobin disorders, including beta-thalassemia (BT) and sickle-cell disease (SCD), are the most common monogenic diseases worldwide, with a global carrier frequency of over 5%.1 With migration, they are becoming more common worldwide, making their management and care an increasing concer...

Disgrifiad llawn

Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Cyhoeddwyd yn:Mediterr J Hematol Infect Dis
Prif Awduron: Motta, Irene, Ghiaccio, Valentina, Cosentino, Andrea, Breda, Laura
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: Università Cattolica del Sacro Cuore 2019
Pynciau:
Review Article
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC6827604/
https://ncbi.nlm.nih.gov/pubmed/31700592
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2019.067
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