Curing Hemoglobinopathies: Challenges and Advances of Conventional and New Gene Therapy Approaches

Inherited hemoglobin disorders, including beta-thalassemia (BT) and sickle-cell disease (SCD), are the most common monogenic diseases worldwide, with a global carrier frequency of over 5%.1 With migration, they are becoming more common worldwide, making their management and care an increasing concer...

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Detalles Bibliográficos
Publicado en:Mediterr J Hematol Infect Dis
Main Authors: Motta, Irene, Ghiaccio, Valentina, Cosentino, Andrea, Breda, Laura
Formato: Artigo
Idioma:Inglês
Publicado: Università Cattolica del Sacro Cuore 2019
Assuntos:
Review Article
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6827604/
https://ncbi.nlm.nih.gov/pubmed/31700592
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2019.067
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