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A novel SUCLA2 mutation presenting as a complex childhood movement disorder

SUCLA2 defects have been associated with mtDNA depletion and the triad of hypotonia, dystonia/Leigh-like syndrome, and deafness. A 9-year-old Brazilian boy of consanguineous parents presented with psychomotor delay, deafness, myopathy, ataxia, and chorea. Despite the prominent movement disorder, bra...

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Detalhes bibliográficos
Publicado no:J Child Neurol
Main Authors: Garone, Caterina, Gurgel-Giannetti, Juliana, Sanna-Cherchi, Simone, Krishna, Sindu, Naini, Ali, Quinzii, Catarina M, Hirano, Michio
Formato: Artigo
Idioma:Inglês
Publicado em: 2016
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6815879/
https://ncbi.nlm.nih.gov/pubmed/27651038
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/0883073816666221
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