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ACTA1-myopathy with prominent finger flexor weakness and rimmed vacuoles

Actinopathy is a group of clinically and pathologically heterogeneous myopathies due to mutations in the skeletal muscle sarcomeric α-actin 1-encoding gene (ACTA1). Disease-onset spans from prenatal life to adulthood and weakness can preferentially affect proximal or distal muscles. Myopathological...

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Detalles Bibliográficos
Publicado en:Neuromuscul Disord
Autores principales: Liewluck, Teerin, Niu, Zhiyv, Moore, Steven A., Alsharabati, Mohammad, Milone, Margherita
Formato: Artigo
Lenguaje:Inglês
Publicado: 2019
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6812538/
https://ncbi.nlm.nih.gov/pubmed/30987788
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nmd.2019.02.012
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