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Gene Editing Preserves Visual Functions in a Mouse Model of Retinal Degeneration

Inherited retinal dystrophies (IRDs) are a large and heterogeneous group of degenerative diseases caused by mutations in various genes. Given the favorable anatomical and immunological characteristics of the eye, gene therapy holds great potential for their treatment. Our goal is to validate the pre...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Front Neurosci
Egile Nagusiak: Vagni, Paola, Perlini, Laura E., Chenais, Naïg A. L., Marchetti, Tommaso, Parrini, Martina, Contestabile, Andrea, Cancedda, Laura, Ghezzi, Diego
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Frontiers Media S.A. 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6748340/
https://ncbi.nlm.nih.gov/pubmed/31551698
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fnins.2019.00945
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