Caricamento...

Therapeutic landscape for Batten disease: current treatments and future prospects

Batten disease (also known as neuronal ceroid lipofuscinoses) constitutes a family of devastating lysosomal storage disorders that collectively represent the most common inherited paediatric neurodegenerative disorders worldwide. Batten disease can result from mutations in 1 of 13 genes. These mutat...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Nat Rev Neurol
Autori principali: Johnson, Tyler B., Cain, Jacob T., White, Katherine A., Ramirez-Montealegre, Denia, Pearce, David A., Weimer, Jill M.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2019
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6681450/
https://ncbi.nlm.nih.gov/pubmed/30783219
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41582-019-0138-8
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !