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Population data improves variant interpretation in autosomal dominant polycystic kidney disease

PURPOSE: Autosomal dominant polycystic kidney disease (ADPKD) is a common adult-onset monogenic disorder, with prevalence of 1/1000. Population databases including ExAC have improved pathogenic variant prioritization in many diseases. Due to pseudogene homology of PKD1, the predominant ADPKD disease...

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Udgivet i:Genet Med
Main Authors: Mallawaarachchi, Amali C., Furlong, Timothy J., Shine, John, Harris, Peter C., Cowley, Mark J.
Format: Artigo
Sprog:Inglês
Udgivet: 2018
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC6677146/
https://ncbi.nlm.nih.gov/pubmed/30369598
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41436-018-0324-x
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