Long-term outcome and unmet needs in infantile-onset Pompe disease

Samankaltaisia teoksia

• Cognitive and academic outcomes in long-term survivors of infantile-onset Pompe disease: A longitudinal follow-up
  Tekijä: Spiridigliozzi, Gail A., et al.
  Julkaistu: (2017)
• The Outcome of Infantile Onset Pompe Disease in South of Iran
  Tekijä: Moravej, Hossein, et al.
  Julkaistu: (2016)
• Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
  Tekijä: Anne Schänzer, et al.
  Julkaistu: (2017-09-01)
• Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
  Tekijä: Schänzer, Anne, et al.
  Julkaistu: (2017)
• The emerging phenotype of long-term survivors with infantile Pompe disease
  Tekijä: Prater, Sean N., et al.
  Julkaistu: (2012)