Učitavanje...

Routine Cerebrospinal Fluid Cytology Reveals Unique Inclusions in Macrophages During Treatment With Nusinersen

Background: Spinal muscular atrophy (SMA) is an autosomal recessive neurodegenerative disorder characterized by degeneration of spinal motor neurons leading to muscular weakness. The antisense oligonucleotide nusinersen was approved for the treatment of patients with 5q-associated SMA. Treatment mus...

Cijeli opis

Spremljeno u:
Bibliografski detalji
Izdano u:Front Neurol
Glavni autori: Gingele, Stefan, Hümmert, Martin W., Alvermann, Sascha, Jendretzky, Konstantin F., Bönig, Lena, Brieskorn, Marina, Schwenkenbecher, Philipp, Sühs, Kurt-Wolfram, Müschen, Lars H., Osmanovic, Alma, Schreiber-Katz, Olivia, Stangel, Martin, Petri, Susanne, Skripuletz, Thomas
Format: Artigo
Jezik:Inglês
Izdano: Frontiers Media S.A. 2019
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6637748/
https://ncbi.nlm.nih.gov/pubmed/31354609
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fneur.2019.00735
Oznake: Dodaj oznaku
Bez oznaka, Budi prvi tko označuje ovaj zapis!