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Congenital Erythropoietic Porphyria: Recent Advances

Congenital erythropoietic porphyria (CEP) is a rare autosomal recessive disorder characterized by photosensitivity and by hematologic abnormalities in affected individuals. CEP is caused by mutations in the uroporphyrinogen synthase (UROS) gene. In three reported cases, CEP has been associated with...

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Publicat a:Mol Genet Metab
Autors principals: Erwin, Angelika L., Desnick, Robert J.
Format: Artigo
Idioma:Inglês
Publicat: 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6597325/
https://ncbi.nlm.nih.gov/pubmed/30685241
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgme.2018.12.008
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