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How I manage children with Diamond‐Blackfan anaemia
Diamond‐Blackfan anaemia (DBA) is a rare inherited marrow failure disorder, characterized by hypoplastic anaemia, congenital anomalies and a predisposition to cancer as a result of ribosomal dysfunction. Historically, treatment is based on glucocorticoids and/or blood transfusions, which is accompan...
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| Publicado en: | Br J Haematol |
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| Main Authors: | , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado: |
John Wiley and Sons Inc.
2018
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| Assuntos: | |
| Acceso en liña: | https://ncbi.nlm.nih.gov/pmc/articles/PMC6587714/ https://ncbi.nlm.nih.gov/pubmed/30515771 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/bjh.15701 |
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