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Accessibility of drugs for rare diseases in China: Policies and current situation

"Poor accessibility to drugs" is the most problematic issue for patients with rare diseases in China. In recent years, China has issued a number of policies, such as prioritizing speeding up the evaluation for rare disease drugs, publishing national rare disease lists and giving priority t...

Disgrifiad llawn

Wedi'i Gadw mewn:
Manylion Llyfryddiaeth
Cyhoeddwyd yn:Intractable Rare Dis Res
Prif Awduron: Yang, Yan, Kang, Qi, Hu, Jiahao, Kong, Fanxin, Tang, Mi, He, Jiangjiang, Jin, Chunlin
Fformat: Artigo
Iaith:Inglês
Cyhoeddwyd: International Research and Cooperation Association for Bio & Socio-Sciences Advancement 2019
Pynciau:
Mynediad Ar-lein:https://ncbi.nlm.nih.gov/pmc/articles/PMC6557233/
https://ncbi.nlm.nih.gov/pubmed/31218157
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.5582/irdr.2019.01068
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