OR13-4 Safety Profile of Asfotase Alfa Treatment of Patients with Hypophosphatasia: A Pooled Analysis

Asfotase alfa (AA), an enzyme replacement therapy, is the only approved medical treatment for pediatric-onset hypophosphatasia (HPP). We report the safety profile of AA in patients from the clinical trial program. Safety data were pooled from 4 open-label, multicenter studies in children age ≤3 year...

Full description

Saved in:
Bibliographic Details
Published in:J Endocr Soc
Main Authors: Whyte, Michael, Bishop, Nick, Hasan, Jawad, Hofmann, Christine, Högler, Wolfgang, Rockman-Greenberg, Cheryl, Sena, Veruska, Zhou, Shanggen, Kishnani, Priya
Format: Artigo
Language:Inglês
Published: Endocrine Society 2019
Subjects:
Bone and Mineral Metabolism
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC6555060/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1210/js.2019-OR13-4
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items