OR13-4 Safety Profile of Asfotase Alfa Treatment of Patients with Hypophosphatasia: A Pooled Analysis

Asfotase alfa (AA), an enzyme replacement therapy, is the only approved medical treatment for pediatric-onset hypophosphatasia (HPP). We report the safety profile of AA in patients from the clinical trial program. Safety data were pooled from 4 open-label, multicenter studies in children age ≤3 year...

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Veröffentlicht in:J Endocr Soc
Hauptverfasser: Whyte, Michael, Bishop, Nick, Hasan, Jawad, Hofmann, Christine, Högler, Wolfgang, Rockman-Greenberg, Cheryl, Sena, Veruska, Zhou, Shanggen, Kishnani, Priya
Format: Artigo
Sprache:Inglês
Veröffentlicht: Endocrine Society 2019
Schlagworte:
Bone and Mineral Metabolism
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC6555060/
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1210/js.2019-OR13-4
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