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Developing ABEmax-NG with Precise Targeting and Expanded Editing Scope to Model Pathogenic Splice Site Mutations In Vivo

RNA splicing is related to many human diseases; however, lack of efficient genetic approaches to modulate splicing has prevented us from dissecting their functions in human diseases. Recently developed base editors (BEs) offer a new strategy to modulate RNA splicing by converting conservative splice...

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Dettagli Bibliografici
Pubblicato in:iScience
Autori principali: Huang, Shisheng, Liao, Zhaodi, Li, Xiangyang, Liu, Zhen, Li, Guanglei, Li, Jianan, Lu, Zongyang, Zhang, Yu, Li, Xiajun, Ma, Xu, Sun, Qiang, Huang, Xingxu
Natura: Artigo
Lingua:Inglês
Pubblicazione: Elsevier 2019
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6548941/
https://ncbi.nlm.nih.gov/pubmed/31130518
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.isci.2019.05.008
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