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ATP13A2 missense variant in Australian Cattle Dogs with late onset neuronal ceroid lipofuscinosis

The neuronal ceroid lipofuscinoses (NCLs) are lysosomal storage disorders characterized by progressive neurodegeneration and declines in neurological functions. Pathogenic sequence variants in at least 13 genes underlie different forms of NCL, almost all of which are recessively inherited. To date 1...

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Dettagli Bibliografici
Pubblicato in:Mol Genet Metab
Autori principali: Schmutz, Isabelle, Jagannathan, Vidhya, Bartenschlager, Florian, Stein, Veronika M., Gruber, Achim D., Leeb, Tosso, Katz, Martin L.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2019
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6548654/
https://ncbi.nlm.nih.gov/pubmed/30956123
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgme.2018.11.015
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