Cargando...

Inotersen: new promise for the treatment of hereditary transthyretin amyloidosis

Hereditary transthyretin amyloidosis is a fatal autosomal dominant disorder characterized by deposition of transthyretin amyloid into the peripheral nervous system, heart, kidney, and gastrointestinal tract. Previous treatments using liver transplantation and small molecule stabilizers were not effe...

Descrición completa

Gardado en:
Detalles Bibliográficos
Publicado en:Drug Des Devel Ther
Main Authors: Mathew, Veena, Wang, Annabel K
Formato: Artigo
Idioma:Inglês
Publicado: Dove Medical Press 2019
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6507904/
https://ncbi.nlm.nih.gov/pubmed/31118583
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2147/DDDT.S162913
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!