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Genotype and phenotype classification of 29 patients affected by Krabbe disease

Krabbe disease is a rare neurodegenerative lysosomal storage disorder caused by mutations in the galactocerebrosidase gene, GALC. Krabbe disease usually affects infants, but has also been reported in older children and adults. Different phenotypes are described based on age at onset. The gene encodi...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:JIMD Rep
Egile Nagusiak: Madsen, Anna M. H., Wibrand, Flemming, Lund, Allan M., Ek, Jakob, Dunø, Morten, Østergaard, Elsebet
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: John Wiley & Sons, Inc. 2019
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6498822/
https://ncbi.nlm.nih.gov/pubmed/31240153
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jmd2.12007
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