Carregant...

Menkes Disease with Discordant Phenotype in Female Monozygotic Twins

Menkes disease (MD) is a rare X-linked recessive disorder caused by mutations in the ATP7A gene. This neurodegenerative disorder typically affects males and is characterized by impaired copper distribution and the malfunction of several copper-dependent enzymes. We report clinically discordant femal...

Descripció completa

Guardat en:
Dades bibliogràfiques
Publicat a:Am J Med Genet A
Autors principals: Burgemeister, Anna Lena, Zirn, Birgit, Oeffner, Frank, Kaler, Stephen G., Lemm, Gunther, Rossier, Eva, Büttel, Hans-Martin
Format: Artigo
Idioma:Inglês
Publicat: 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6475897/
https://ncbi.nlm.nih.gov/pubmed/26239182
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.a.37276
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!