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A Case of Hypotonia-Cystinuria Syndrome With Genito-Urinary Malformations and Extrarenal Involvement

Hypotonia-Cystinuria syndrome (HCS) is a rare disease, caused by a mutation in two contiguous genes (SLC3A1 and PREPL) localized on chromosome 2p21, and it is characterized by both renal involvement with cystine stones and nervous involvement with hypotonia. We here describe a 2 years old child with...

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Detalhes bibliográficos
Publicado no:Front Pediatr
Main Authors: Taroni, Francesca, Capone, Valentina, Berrettini, Alfredo, De Marco, Erika Adalgisa, Manzoni, Gian Antonio, Montini, Giovanni
Formato: Artigo
Idioma:Inglês
Publicado em: Frontiers Media S.A. 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6465885/
https://ncbi.nlm.nih.gov/pubmed/31024870
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fped.2019.00127
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