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Successful donor engraftment and repair of the blood-brain barrier in cerebral adrenoleukodystrophy

Adrenoleukodystrophy (ALD) is caused by mutations within the X-linked ABCD1 gene, resulting in the inability to transport acylated very long chain fatty acids (VLCFAs) into the peroxisome for degradation. VLCFAs subsequently accumulate in tissues, including the central nervous system. Up to 40% of b...

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Detalhes bibliográficos
Publicado no:Blood
Main Authors: Orchard, Paul J., Nascene, David R., Miller, Weston P., Gupta, Ashish, Kenney-Jung, Dan, Lund, Troy C.
Formato: Artigo
Idioma:Inglês
Publicado em: American Society of Hematology 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6440119/
https://ncbi.nlm.nih.gov/pubmed/30635285
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2018-11-887240
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