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Luspatercept improves hemoglobin levels and blood transfusion requirements in a study of patients with β-thalassemia

β-thalassemia is a hereditary disorder with limited approved treatment options; patients experience anemia and its complications, including iron overload. The study aim was to determine whether luspatercept could improve anemia and disease complications in patients with β-thalassemia. This open-labe...

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Detalhes bibliográficos
Publicado no:Blood
Main Authors: Piga, Antonio, Perrotta, Silverio, Gamberini, Maria Rita, Voskaridou, Ersi, Melpignano, Angela, Filosa, Aldo, Caruso, Vincenzo, Pietrangelo, Antonello, Longo, Filomena, Tartaglione, Immacolata, Borgna-Pignatti, Caterina, Zhang, Xiaosha, Laadem, Abderrahmane, Sherman, Matthew L., Attie, Kenneth M.
Formato: Artigo
Idioma:Inglês
Publicado em: American Society of Hematology 2019
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6440118/
https://ncbi.nlm.nih.gov/pubmed/30617198
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2018-10-879247
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