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The use of luspatercept for thalassemia in adults

Luspatercept is an activin receptor ligand trap that has been shown to enhance late-stage erythropoiesis in animal models of β-thalassemia. A multicenter, international, phase 2 dose-finding study was initiated in adult patients with β-thalassemia, either non–transfusion-dependent thalassemia (NTDT)...

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Bibliografske podrobnosti
izdano v:Blood Adv
Main Authors: Cappellini, Maria Domenica, Taher, Ali T.
Format: Artigo
Jezik:Inglês
Izdano: American Society of Hematology 2021
Teme:
Online dostop:https://ncbi.nlm.nih.gov/pmc/articles/PMC7805339/
https://ncbi.nlm.nih.gov/pubmed/33570654
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/bloodadvances.2020002725
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