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Cystic fibrosis transmembrane conductance regulator modulators: precision medicine in cystic fibrosis

PURPOSE OF REVIEW: The aim of this study was to describe the newest development in cystic fibrosis (CF) care, CF transmembrane conductance regulator (CFTR) modulator therapies. RECENT FINDINGS: Phase II results showing CFTR modulator triple therapies are more effective than current CFTR modulators....

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Detalhes bibliográficos
Publicado no:Curr Opin Pediatr
Main Authors: Burgener, Elizabeth B., Moss, Richard B.
Formato: Artigo
Idioma:Inglês
Publicado em: 2018
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6398332/
https://ncbi.nlm.nih.gov/pubmed/29538046
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/MOP.0000000000000627
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