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Duchenne Muscular Dystrophy: From Diagnosis to Therapy

Duchenne muscular dystrophy (DMD) is an X-linked inherited neuromuscular disorder due to mutations in the dystrophin gene. It is characterized by progressive muscle weakness and wasting due to the absence of dystrophin protein that causes degeneration of skeletal and cardiac muscle. The molecular di...

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Dades bibliogràfiques
Publicat a:Molecules
Autors principals: Falzarano, Maria Sofia, Scotton, Chiara, Passarelli, Chiara, Ferlini, Alessandra
Format: Artigo
Idioma:Inglês
Publicat: MDPI 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6332113/
https://ncbi.nlm.nih.gov/pubmed/26457695
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/molecules201018168
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