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Emerging microRNA Therapeutic Approaches for Cystic Fibrosis

Cystic fibrosis (CF) is caused by mutations in the cystic fibrosis transmembrane conductance regulator (CFTR) gene and remains the most common life-shortening diseases affecting the exocrine organs. The absence of this channel results in an imbalance of ion concentrations across the cell membrane an...

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Publicado en:Front Pharmacol
Autores principales: Bardin, Pauline, Sonneville, Florence, Corvol, Harriet, Tabary, Olivier
Formato: Artigo
Lenguaje:Inglês
Publicado: Frontiers Media S.A. 2018
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6186820/
https://ncbi.nlm.nih.gov/pubmed/30349480
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fphar.2018.01113
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