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Dysarthria and Stutter as Presenting Symptoms of Late‐Onset Tay‐Sachs Disease in Three Siblings

Late‐onset Tay‐Sachs disease (LOTS) is a rare autosomal‐recessive genetic disorder caused by insufficient activity of the lysosomal enzyme, beta‐hexosaminidase A, resulting in intracellular accumulation of gangliosides in the central nervous system. Clinical manifestations can include unsteadiness i...

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Dettagli Bibliografici
Pubblicato in:Mov Disord Clin Pract
Autori principali: Grim, Kristina K., Phillips, Gregory D., Renner, David R.
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley and Sons Inc. 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6178690/
https://ncbi.nlm.nih.gov/pubmed/30363497
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mdc3.12194
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