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A first CLN6 variant case of late infantile neuronal ceroid lipofuscinosis caused by a homozygous mutation in a boy from China: a case report

BACKGROUND: Neuronal ceroid lipofuscinosis (NCLs) are lysosomal storage disorders characterized by seizures, motor impairment, and loss of vision. Ceroid lipofuscinosis (CLN) gene mutations are the cause, but NCL cases arising from CLN6 mutations have not been described in China to date. The CLN6 pr...

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Detalhes bibliográficos
Publicado no:BMC Med Genet
Main Authors: Sun, Guilian, Yao, Fang, Tian, Zhuoling, Ma, Tianjiao, Yang, Zhiliang
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2018
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC6167792/
https://ncbi.nlm.nih.gov/pubmed/30285654
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12881-018-0690-x
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