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Peptide Nucleic Acids as miRNA Target Protectors for the Treatment of Cystic Fibrosis

Cystic Fibrosis (CF) is one of the most common life shortening conditions in Caucasians. CF is caused by mutations in the CF Transmembrane Conductance Regulator (CFTR) gene which result in reduced or altered CFTR functionality. Several microRNAs (miRNAs) downregulate the expression of CFTR, thus cau...

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Dettagli Bibliografici
Pubblicato in:Molecules
Autori principali: Zarrilli, Federica, Amato, Felice, Morgillo, Carmine Marco, Pinto, Brunella, Santarpia, Giuliano, Borbone, Nicola, D’Errico, Stefano, Catalanotti, Bruno, Piccialli, Gennaro, Castaldo, Giuseppe, Oliviero, Giorgia
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC6152032/
https://ncbi.nlm.nih.gov/pubmed/28698463
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/molecules22071144
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