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Burden of Illness in Acid Sphingomyelinase Deficiency: A Retrospective Chart Review of 100 Patients

Acid sphingomyelinase deficiency (ASMD) is a rare, progressive, and often fatal lysosomal storage disease caused by the deficiency of the enzyme acid sphingomyelinase (ASM) resulting in accumulation of sphingomyelin in target tissues. Little is known regarding predictors of disease-related morbidity...

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Podrobná bibliografie
Vydáno v:JIMD Rep
Hlavní autoři: Cox, Gerald F., Clarke, Lorne A., Giugliani, Roberto, McGovern, Margaret M.
Médium: Artigo
Jazyk:Inglês
Vydáno: Springer Berlin Heidelberg 2018
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC6122055/
https://ncbi.nlm.nih.gov/pubmed/29995201
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2018_120
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